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Agalsidase-Beta Therapy for Advanced Fabry Disease: A Randomized Trial
Maryam Banikazemi, MD; Jan Bultas, MD, PhD; Stephen Waldek, MB, BCh; William R. Wilcox, MD, PhD; Chester B. Whitley, PhD, MD; Marie McDonald, MD; Richard Finkel, MD; Seymour Packman, MD; Daniel G. Bichet, MD; David G. Warnock, MD; Robert J. Desnick, PhD, MD; Fabry Disease Clinical Trial Study Group*
Annals of Internal Medicine 2007;146:77-86.
doi:10.7326/0003-4819-146-2-200701160-00148
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